My brother was born with Spinal Muscular Atrophy. He never walked, and was dependent on his electric wheelchair.

Trussville community raises money for 7-year-old with Spinal Muscular Dystrophy Non Sequitur by Wiley Miller 3 Accounts Rich People Keep Money in That You Should Too Supreme Court upholds key ...

This year’s ride is supporting the Moore family. 7-year-old Margaux Moore has spinal muscular dystrophy. “It’s amazing to see the community riled up, with us, supporting us, showing us so ...

Andrew Fein, an analyst from H.C. Wainwright, reiterated the Buy rating on Catalyst Pharma (CPRX – Research Report). The associated price ...

Explore the role and challenges of AAV characterization, the significance of capsid filling, and the best methods to enhance gene therapy.

Windsor Paralympic champion, Danielle Campo, has been crowned the number one Inspirational Speaker of the Year for 2024 at ...

"My daughter has a rare form of muscular dystrophy called spinal muscular atrophy. She's the only one in this area that we know, so she doesn't know any other kids. When she gets the right age ...

Interestingly, SmD1 is a survival of motor neuron (SMN) complex component. SMN dysfunction is implicated in spinal muscular ...

Jackie Apostel, 29, shared a photo of the wound, taken shortly after she underwent surgery for an undisclosed spinal issue, ...

And I think another large part is that with these types of therapies compared to maybe other gene therapies in Duchenne muscular dystrophy or spinal muscular atrophy [SMA], you have progressive ...

“Often, they may even undergo unnecessary testing and unnecessary surgeries — carpal tunnel releases, spinal surgeries ... Academy of Neurology, Muscular Dystrophy Association, OrphAI ...