Muscular Dystrophy News1d
Sarepta stops development of exon 51-skipping therapy for DMD
Sarepta has stopped developing SRP-5051, its exon 51-skipping therapy for Duchenne MD, due to long-term safety concerns and ...
Muscular Dystrophy News5d
The missed milestones in the teenage years because of DMD
Columnist Betty Vertin wishes she could take away the pain over the milestones in the teenage years her sons with DMD will miss.
Muscular Dystrophy News6d
Patients with certain mutations lose their walking ability earlier: Study
Specific mutations in the DMD gene influence how long patients retain the ability to walk, even when treated with ...