Three years after Elevidys treatment, boys with DMD show sustained motor function compared with expected disease progression.

An accessibility tool allows columnist Robin Stemple to keep making music. It's an example of how help from friends can jog ...

Life with Duchenne MD rarely follows a neat arc, writes columnist. That forces people to revisit the script and constantly ...

Leaders with CureDuchenne say approvals are expected this year for several new treatments for Duchenne MD, making it "an ...

An international team of scientists has designed a new type of therapy to target the mutant toxic RNA that causes myotonic ...

What is strength? Columnist Patrick Moeschen believes it's the act of persevering through events that are beyond our control.

The U.S. Food and Drug Administration has awarded orphan drug status to Atossa Therapeutics' (Z)-endoxifen for Duchenne ...

All muscular dystrophies cause muscle weakness, but life expectancy can vary dramatically between types of muscular dystrophy.

Navigating Duchenne muscular dystrophy (DMD) is a journey with challenges at every stage. From recognizing early signs to managing daily life, understanding genetics and heart health is key. With the ...

My family and I are part of a community of boys, men, and families living with Duchenne muscular dystrophy. That community extends far beyond the U.S., where we live. Families uniquely experience ...

With her youngest son with Duchenne now using a power wheelchair at home, columnist Betty Vertin thinks her family has outgrown their house.