PROGRESSIVE muscular dystrophy was recognized over a century ago, and Gowers noted ... shown to occur in the Duchenne type of muscular dystrophy before any detectable signs of muscle weakness ...
STAT+ subscribers can sign up here to get it delivered to their inbox. The EMBARK Phase 3 study for Elevidys, Sarepta Therapeutics’ gene therapy for Duchenne muscular dystrophy, was published ...
Phase 2 results with Wave Life Sciences' Duchenne muscular dystrophy candidate WVE-N531 ... FORWARD-53 also revealed signs of improved muscle health in DMD patients, including increases in muscle ...
For comparison of the three patients harboring two null alleles (age 48 ± 17 years), we included five clinically matched patients with Becker muscular dystrophy (BMD) (age 31 ± 16 years ...
Kuntz, MD, was a fellow about 45 years ago, there were few more devastating diagnoses than Duchenne muscular dystrophy (DMD).
Zinc supplementation showed limited benefits in improving muscle health and hydration in boys with DMD. Nearly 30% of participants had low zinc levels initially, with slight improvement post ...
Sarepta Therapeutics has decided not to continue the development of vesleteplirsen, a follow-up to its Duchenne muscular dystrophy (DMD) therapy Exondys 51. The drug – formerly known as SRP-5051 ...
Jefferies has initiated coverage of Sarepta Therapeutics (NASDAQ:SRPT) at buy saying its Duchenne muscular dystrophy franchise represents a $4B+ opportunity, as well as a strong pipeline and ...
We recently published a list of 10 Biggest Stocks with Negative Beta to Consider. In this article, we are going to take a look at where Wave Life Sciences (NASDAQ:WVE) stands against other biggest ...
Sarepta Therapeutics has ended development of a late-phase Duchenne muscular dystrophy (DMD) drug candidate over a safety problem. The safety signal deprived Sarepta of a near-term shot at accelerated ...
Nathan Benham is raising funds for Muscular Dystrophy UK. For over 60 years, the charity has built a community bringing together family and friends with healthcare professionals and scientists to ...