CK-089 has a different chemical structure from previously developed FSTAs and in preclinical research, has been observed to have ... and function in a mouse model with a specific type of muscular ...

Analyst Joseph Schwartz from Leerink Partners maintained a Buy rating on Solid Biosciences (SLDB – Research Report) and keeping the price ...

However, this is not the first time that the monkeys escaped the facility. In 2016, 19 monkeys escaped from Alpha Genesis and ...

Despite diagnostic and therapeutic advances, mortality and the multi-systemic health impact of SMA continue to be experienced ...

Kuntz, MD, was a fellow about 45 years ago, there were few more devastating diagnoses than Duchenne muscular dystrophy (DMD .

Researchers created a mouse model to study liver symptoms of myotonic dystrophy type 1, revealing how toxic RNA in the liver ...

The $514,000 DOD award will be used to study the efficacy of gene editors in the treatment of Duchenne Muscular Dystrophy.

Caregivers of both adults and children with Duchenne muscular dystrophy (DMD) face significant disruptions to their work productivity and personal lives, underscoring the need for better treatments ...

His commitment to the Muscular Dystrophy Association and the families ... MDA is dedicated to accelerating research, supporting multidisciplinary care throughout its network of over 150 MDA ...

Spinal muscular atrophy (SMA) is a disorder affecting the motor neurons—nerve cells that control voluntary muscle movement. These cells are located in the spinal cord. Because the muscles cannot ...

As part of that job, I’m also a caregiver to Max, Rowen, and Charlie, who all have Duchenne muscular dystrophy (DMD). Additionally, I’m a chronic DIYer (do-it-yourselfer). Yes, you read that correctly ...