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Calves to Cure helps fund research for Montana boy's rare disease
The Billings Livestock Commission hosted the sixth annual Calves to Cure to help raise money and awareness for Duchenne ...
'The Remarkable Life of Ibelin' review: A remarkable doc about a 'World of Warcraft' player's inner life
The Remarkable Life of Ibelin blends traditional documentary techniques with World of Warcraft recreations to paint a ...
Doctors Said These Women’s Mutated Genes Wouldn’t Harm Them
The embryos were female, and Jenssen remembers the doctors assuring her that, because the Duchenne mutation is linked to the ...
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Calves to Cure helps fund research for Worden boy's rare disease
The Billings Livestock Commission hosted the sixth annual Calves to Cure on Thursday, an event to help raise money and ...
Muscular Dystrophy News3d
DMD treatment SMT-M01 gets FDA orphan drug, rare disease tags
DMD treatment SMT-01, a cell replacement therapy, received FDA orphan drug and rare pediatric disease designations.
New Hampshire Union Leader3dOpinion
Lisa D. Beaudoin: ADA regulations only help the disabled if enforced
AN INCIDENT in front of Williams Sonoma at Salem’s Tuscan Village highlights the persistent issue of systemic ableism in New ...
Finger Lakes Times4d
Suneel's partners with Jett Foundation to support NY families caring for loved one with Duchenne Muscular Dystrophy
To provide hope for families grappling with Duchenne muscular dystrophy across Upstate New York, Buffalo-based Suneel’s Light Foundation has launched a new community grant program, Brighter Days Commu ...
biopharma-reporter4d
FDA designations boost AI-driven cell therapy approach for Duchenne muscular dystrophy
The FDA has granted Orphan Drug and Rare Pediatric Disease Designations to Somite’s cell replacement therapy for the ...
News Letter on MSN4d
Northern Ireland man with progressive muscle wasting disease Duchenne Muscular Dystrophy appeals for help to secure holiday accomodation for local families
A Northern Ireland man, 31, with Duchenne Muscular Dystrophy – a progressive muscle wasting disease that affects skeletal ...
FDA backs Somite.ai's new drug for rare children's muscle disease
AI-driven biotech Somite.ai scores dual FDA designations for its novel treatment, potentially fast-tracking hope for families ...
Muscular Dystrophy News4d
Why patient advocacy is important for those of us with Duchenne
Whether it’s migrant workers, people ... Muscular Dystrophy News Today, SPAN, and other platforms that allow me to express ...
The Pharma Letter5d
Capricor rises as it expands deal with Nippon Shinyaku
US biotech Capricor Therapeutics has entered into a binding term sheet with Japanese drugmaker Nippon Shinyaku for the ...