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    Who owns Duchenne muscular dystrophy therapy?
    Deals and Financings Japan’s Nippon Shinyaku (OTCPK:NPNKF, OTCPK:NPPNY) will acquire European rights for a Duchenne muscular dystrophy disease therapy developed by Capricor Therapeutics (CAPR) of San Diego (see story).

    Week In Review: Nippon Shinyaku Signs $735m Deal For DMD Therapy

    seekingalpha.com
    What if a girl had a Duchenne mutation?
    The embryos were female, and Jenssen remembers the doctors assuring her that, because the Duchenne mutation is linked to the X chromosome, a girl who carried it would have a backup chromosome, with a working copy of the affected gene, and would be as healthy as Jenssen was.

    These Women Knew Their Genes Were Betraying Them

    msn.com
    Will Nippon Shinyaku acquire European rights for Duchenne muscular dystrophy therapy?
    Play(4min) Summary Nippon Shinyaku will acquire European rights for a Duchenne muscular dystrophy disease therapy developed by Capricor Therapeutics of San Diego. Shanghai Fosun Pharma announced plans to buy out its JV partner, Kite Pharma, gaining full control of the JV’s two CAR-T products in China.

    Week In Review: Nippon Shinyaku Signs $735m Deal For DMD Therapy

    seekingalpha.com
    Should the field use multiple drugs to treat Duchenne muscular dystrophy?
    “The field should use multiple drugs to address the disease from all different levels.” Duchenne muscular dystrophy, also known as DMD, is a rare genetic neurodegenerative disorder causing progressive muscle loss, primarily in young boys.

    Duchenne muscular dystrophy: major trials and events to watch in 2023

    msn.com
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  3. The US Food and Drug Administration has given the green light for the first gene therapy that treats a rare form of muscular dystrophy to be used in most people who have the disease and a certain genetic mutation.

    FDA expands approval of first gene therapy for rare form of muscu…

    www.cnn.com/2024/06/20/health/fda-gene-therapy-duchenne-muscular-dystrophy/index.html
    www.cnn.com/2024/06/20/health/fda-gene-therapy-duchenne-muscular-dystrop…
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  4. CNN
    https://www.cnn.com/2024/06/20/health/fda-gene...

    FDA expands approval of first gene therapy for rare form of …

  5. NPR
    https://www.npr.org/sections/health-shots/2023/06/...

    Muscular dystrophy patients get first gene therapy - NPR

  7. CNN
    https://www.cnn.com/2023/06/22/health/fda-sarepta...

    FDA approves $3.2 million gene therapy for rare muscular …

  8. CNN
    https://www.cnn.com/2023/05/12/health/duchenne...

    FDA advisers narrowly vote in favor of experimental gene therapy …

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    Duchenne muscular dystrophy
    Gene therapy
  9. Food and Drug Administration (.gov)
    https://www.fda.gov/news-events/press...

    FDA Approves First Gene Therapy for Treatment of Certain …

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    Duchenne muscular dystrophy
    Gene therapy

  10. Explore duchenne muscular dystrophy news

  11. Food and Drug Administration (.gov)
    https://www.fda.gov/news-events/press...

    FDA Expands Approval of Gene Therapy for Patients with …

    Tags:
    Duchenne muscular dystrophy
    Gene therapy
  12. NPR
    https://www.npr.org/sections/health-shots/…

    FDA Duchenne muscular dystrophy gene therapy : …

    WEBMay 12, 2023 · A panel of experts voted 8-6 in favor of Food and Drug Administration approval of the first gene therapy for Duchenne muscular dystrophy, a fatal genetic disease.

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    Duchenne muscular dystrophy
    Gene therapy
  13. Food and Drug Administration (.gov)
    https://www.fda.gov/news-events/press...

    FDA Approves Nonsteroidal Treatment for Duchenne Muscular …

  14. AP News
    https://apnews.com/article/fda-gene-therapy...

    First gene therapy for deadly form of muscular dystrophy gets FDA ...

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    Duchenne muscular dystrophy
    Gene therapy
    Associated Press
  15. Nature
    https://www.nature.com/articles/d41586 …

    ‘It’s a vote for hope’: first gene therapy for muscular …

    WEBJun 2, 2023 · Update: The US Food and Drug Administration has now approved the first gene therapy for Duchenne muscular dystrophy for children aged four and five. The one-time treatment, named Elevidys, …

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    Duchenne muscular dystrophy
    Gene therapy